Stock Surges Following Positive Clinical Update Shares of Design Therapeutics (NASDAQ:DSGN) climbed 27% on Monday after the ...

Shares of Design Therapeutics jumped after the company reported positive data from a study of its DT-216P2 drug for Friedreich ataxia, a neuromuscular disease. The stock rose 10% to $15.85 in ...

IntraBio Inc., a global biopharmaceutical company focused on developing and commercializing therapies for neurological diseases, today announced that the U.S. Food and Drug Administration (FDA) has ...

Supported by phase 3 trial data showing significant SARA score improvements, levacetylleucine is on track to potentially become the first approved therapy for A-T.

DT-216P2 demonstrated dose-dependent improvement in multiple clinical measures and increases in endogenous frataxin mRNA and protein after four weeks of intravenous dosing DT-216P2 generally ...

Ataxia is a degenerative disease affecting the nervous system, presenting poor coordination and movement, difficulties with speech, walking, fine motor skills, swallowing, and vision. It mainly ...

The trial is designed to evaluate the safety, pharmacokinetics, pharmacodynamics, and exploratory clinical outcomes of ...

Researchers have uncovered a fundamental rule that governs how genes are physically arranged inside the cell nucleus, and how ...

Ataxia is a medical term describing a lack of coordination. Uncoordinated movement is also known as coordination impairment or loss of coordination. For most people, body movements are smooth, ...

Ataxia means the loss of coordination of body movements. Acute cerebellar ataxia is a disorder in children that causes a sudden loss of coordination. It is relatively prevalent in children, especially ...

Ataxia is a lack of muscle coordination that may affect a person’s speech, eye movements, and ability to swallow, walk, and pick up objects. It can happen due to certain health conditions, genetics, ...

The beloved 'Science Guy' says many of his family members suffer from a rare neurological disorder that their ancestors had in colonial times Beloved "Science Guy" Bill Nye is sharing his family's ...