Investigational oral substrate therapy BBP-418 demonstrated significant increases in alpha-dystroglycan glycosylation and improved ambulatory function in the phase 3 FORTIFY interim analysis.

For decades, families have been told there was no cure for Duchenne Muscular Dystrophy, or DMD, a rare genetic condition that causes muscles to weaken over time, and few treatment options. But today, ...

Your muscles need continuous maintenance to stay strong and healthy. Duchenne muscular dystrophy (DMD) happens when there is a change in a person's genetic instructions that affects the production of ...

Analysts homed in on Duchenne muscular dystrophy and myotonic dystrophy type 1 assets during first quarter earnings as major ...

Submission for Accelerated Approval based on dystrophin as a surrogate endpoint - - In the registrational expansion cohort of the DELIVER trial, treatment with z-rostudirsen res ...

The Duchenne muscular dystrophy clinical trial analysis report delivers important insights into ongoing research of 75+ ...

The first gene therapy for children with Duchenne muscular dystrophy has been approved by the U.S. Food and Drug Administration. The therapy can be used in 4- and 5-year-olds with the degenerative ...

Muscular dystrophy (MD) is a group of genetic diseases that cause your muscles to progressively weaken and degenerate. There are several types of MD, each with its own symptoms, but they all involve ...

Learn how to exercise safely with Duchenne muscular dystrophy, for your flexibility, mobility, and overall health, without damaging your muscles.

Conserving energy is an essential component of living with Duchenne muscular dystrophy (DMD). Fatigue, both physical and mental, is extremely common with this genetic disease that causes progressive ...

Myotonic muscular dystrophy, which is sometimes called myotonic dystrophy, is a type of muscular dystrophy. There are two types of myotonic muscular dystrophy, described as type 1 (DM 1) and type 2 ...