The FDA has accepted Scholar Rock's application for regulatory approval of apitegromab for SMA and is expected to have its ...

Columnist Ari Anderson shares how his home-care nurses help to provide him with two things that are vital while living with ...

Children with SMA diagnosed via newborn screening programs typically start treatment earlier and reach more motor milestones, ...

U.K. experts developed consensus guidance to support earlier hip monitoring and individualized care decisions for children ...

A newly approved high-dose Spinraza regimen may offer added SMA treatment benefits, with similar safety findings to the ...

Leaning too far into joy or too deeply into sorrow is unrealistic, writes columnist Connie Chandler, who instead finds ...

In order to provide effective support for others, columnist Kevin Schaefer recognizes the importance of addressing his own ...

Guest writer Amal Khdour shares the story of her son, Hussein, who was born with SMA type 1. He is doing well after receiving ...

A European Medicines Agency panel recommended that the one-time gene therapy Itvisma be approved to treat SMA patients ages 2 ...

SMA is more common in wealthier countries, likely reflecting better diagnostic tools and treatment access, according to a ...

Columinst Helen Baldwin remembers her infant son, Jeffrey, and the difficult months he went through following his diagnosis of SMA type 1.

When forming a new friendship, columnist Connie Chandler hopes others see her first. But don't ignore the wheelchair entirely ...