Keenova Therapeutics plc announced the first-time publication of a retrospective analysis using previously generated XIAFLEX® (collagenase clostridium histolyticum) data. The analysis evaluates ...

"Beast Games" winner Jeff Allen hopes finding a cure for his son's rare disease will unlock new treatments for other brain conditions.

“Yes, doctor. My dad’s first fall was on his 65th birthday. He stood in the driveway and suddenly dropped backwards on his back. After he fell two more times, we came to the clinic.” The symptoms the ...

UniQure needs to run another trial to prove its gene therapy "actually helps people with Huntington's disease," said a senior FDA official.

A “living drug” was developed as a cancer treatment. Now it is showing promise for conditions, such as lupus and multiple sclerosis, that have long been considered incurable.

2:10 Kelowna man first to be cured by gene-editing A doctor at B.C. Children’s Hospital says he was delighted to tell one of his patients that he had been cured of his condition. Nineteen-year-old ...

The Food and Drug Administration (FDA) announced a new proposal Monday for flexible drug approval pathway treatments addressing ultrarare diseases. The FDA unveiled draft guidance on a proposed ...

LONG ISLAND (PIX11) – A Long Island single mother is sharing her 2-year-old daughter’s medical story in hopes of finding a cure for a disease that has caused multiple aneurysms to grow. With the ...

Japan has approved ground-breaking stem-cell treatments for Parkinson's and severe heart failure, one of the manufacturers and media reports said Friday, with the therapies expected to reach patients ...

A nonprofit organization aiming to find a cure for a group of rare genetic skin disorders known as Epidermolysis Bullosa before the end of the decade is gaining ground on its goal by acting like a ...

Yesterday marked day one of the 2026 ASCO Genitourinary (GU) Cancers Symposium, and the updates were full of hope for people with advanced prostate cancer. CURE highlights two studies that are ...

Gepotidacin and nitrofurantoin demonstrate similar efficacy in reducing symptom severity and restoring daily function in women with uncomplicated UTI.