Sarepta Therapeutics said it will voluntarily “and temporarily” pause all shipments of Elevidys® (delandistrogene ...

Highlights of the Sanner facility include a 60,500-sq-ft site equipped with GMP-certified cleanrooms (ISO class 7 & 8) and ...

IL-1 is considered one of the key mediators involved in the pathogenesis of OA, causing inflammation, joint pain, and ...

Using data from the T2T reference, scientists linked two new genes to changes in brain size and synapse signaling.

Prime editing corrects the most common genetic mutations that cause alternating hemiplegia of childhood (AHC), a rare and severe neurological disorder.

This test can be performed on children before their genetic risk starts to shape their weight, which may support early prevention.